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Purple Day® Expo 2025

uniQure

Delivering on the Promise of Gene Therapy
Address

1 Hartwell Ave.
Lexington, MA 02421
United States

Contact

Edgar Vega

[email protected]

562-413-4852

uniQure is delivering on the promise of gene therapy – a single treatment with curative results – through an innovative adeno-associated virus (AAV)-based technology platform supported by proprietary commercial-grade manufacturing. The recent approvals of our gene therapy for hemophilia B – an historic achievement based on more than a decade of research and clinical development – represent a major milestone in the field of genomic medicine and usher in a new treatment approach for patients living with hemophilia. We’re now advancing a clinical program in Huntington’s disease with a growing list of preclinical candidates.

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